GenTIGSA Gene Database on Rare Genetic Disorders

Lists of Rare Genetic Disorders  

Familial Hypercholesterolemia(Hyperbetalipoproteinemia) 
An Autosomal dominant mode(s) within the Metabolic disorders category
Reported Pathogenic variants
Candidate Gene Information
S.No. Name/GeneID Description Cytogentic Band Gene Location on genomic DNA Gene Length Exons Details Gene Cross-References
1 LDLR/3949 low density lipoprotein receptor 19p13.2 Chr19, NC_000019.10
(11089463..11133820)
44358 nt 19 More... OMIM gene
gnomAD browser
EnsEMBL
GeneCards
ClinGen gene

2 PCSK9/255738 proprotein convertase subtilisin/kexin type 9 1p32.3 Chr1, NC_000001.11
(55039548..55064852)
25305 nt 15 More... OMIM gene
gnomAD browser
EnsEMBL
GeneCards
ClinGen gene

3 APOB/338 apolipoprotein B 2p24.1 Chr2, NC_000002.12
(21001429..21044073, complement)
42645 nt 29 More... OMIM gene
gnomAD browser
EnsEMBL
GeneCards
ClinGen gene

4 LDLRAP1/26119 low density lipoprotein receptor adaptor protein 1 1p36.11 Chr1, NC_000001.11
(25543606..25590400)
46795 nt 15 More... OMIM gene
gnomAD browser
EnsEMBL
GeneCards
ClinGen gene

5 PIP5K1B/8395 phosphatidylinositol-4-phosphate 5-kinase type 1 beta 9q21.11 Chr9, NC_000009.12
(68705240..69009176)
303937 nt 21 More... OMIM gene
gnomAD browser
EnsEMBL
GeneCards
ClinGen gene

6 SLC27A2/11001 solute carrier family 27 member 2 15q21.2 Chr15, NC_000015.10
(50182196..50236385)
54190 nt 10 More... OMIM gene
gnomAD browser
EnsEMBL
GeneCards
ClinGen gene

7 INPP5F/22876 inositol polyphosphate-5-phosphatase F 10q26.11 Chr10, NC_000010.11
(119726050..119829147)
103098 nt 29 More... OMIM gene
gnomAD browser
EnsEMBL
GeneCards
ClinGen gene

8 PLCB4/5332 phospholipase C beta 4 20p12.2 Chr20, NC_000020.11
(9068678..9480808)
412131 nt 49 More... OMIM gene
gnomAD browser
EnsEMBL
GeneCards
ClinGen gene

9 ITPR2/3709 inositol 1,4,5-trisphosphate receptor type 2 12p11.23 Chr12, NC_000012.12
(26335352..26833194, complement)
497843 nt 62 More... OMIM gene
gnomAD browser
EnsEMBL
GeneCards
ClinGen gene

10 PIBF1/10464 progesterone immunomodulatory binding factor 1 13q22.1 Chr13, NC_000013.11
(72782133..73016461)
234329 nt 22 More... OMIM gene
gnomAD browser
EnsEMBL
GeneCards
ClinGen gene

11 PLA1A/51365 phospholipase A1 member A 3q13.33 Chr3, NC_000003.12
(119597885..119629811)
31927 nt 13 More... OMIM gene
gnomAD browser
EnsEMBL
GeneCards
ClinGen gene

12 CYP3A4/1576 cytochrome P450 family 3 subfamily A member 4 7q22.1 Chr7, NC_000007.14
(99756967..99784184, complement)
27218 nt 13 More... OMIM gene
gnomAD browser
EnsEMBL
GeneCards
ClinGen gene

13 HACL1/26061 2-hydroxyacyl-CoA lyase 1 3p25.1 Chr3, NC_000003.12
(15560699..15601569, complement)
40871 nt 17 More... OMIM gene
gnomAD browser
EnsEMBL
GeneCards
ClinGen gene

14 APOE/348 apolipoprotein E 19q13.32 Chr19, NC_000019.10
(44905796..44909393)
3598 nt 6 More... OMIM gene
gnomAD browser
EnsEMBL
GeneCards
ClinGen gene

Variant Information             Highlighted rows indicate variants are reported from India
Disorder Cross-References:      OMIM                    GTR          MedGen          MalaCards          EMBL-EBI OLS    Monarch Initiative          NORD     

Patient care services
Clinical Symptoms & Disabilities