GenTIGSA Gene Database on Rare Genetic Disorders

Variants in ClinVar from 539 of 916 Rare Genetic Disorders of GenTIGS

Pyruvate dehydrogenase E1-alpha deficiency

An  X-linked recessive  mode(s) within the Metabolic disorders  category

Conflicting classifications of pathogenicity 1
Likely pathogenic 1
Pathogenic/Likely pathogenic 1

Variant name Variant type GRCH38 location Germline classification Molecular consequence dbSNP_ID Submitter
NM_000284.4(PDHA1):c.522C>T (p.Gly174=) Single nucleotide variant ChrX:19354502 Conflicting classifications of pathogenicity Synonymous variant|intron variant rs769308417 .Diagnostics Services (NGS), CSIR - Centre For Cellular And Molecular Biology
NM_000284.4(PDHA1):c.291+1_418+1dup Duplication ChrX:19350109 - 19350110 Likely pathogenic Splice acceptor variant|splice donor variant .Foundation for Research in Genetics and Endocrinology, FRIGE's Institute of Human Genetics
NM_000284.4(PDHA1):c.379C>T (p.Arg127Trp) Single nucleotide variant ChrX:19351368 Pathogenic/Likely pathogenic Missense variant rs199959402 .Kasturba Medical College, Manipal, Kasturba Medical College, Manipal, Manipal Academy of Higher Education, Manipal, India

Indian Institutes & Variant Submission Overview
Chromosome-wise Variant Distribution