GenTIGSA Gene Database on Rare Genetic Disorders
  Beta Version

Variants from 496 rare genetic disorders, with a total of 857 reported, submitted from India

Pontocerebellar hypoplasia type 1

An  Autosomal recessive  mode(s) within the Neuromuscular disorders  category

Pathogenic 1
Pathogenic/Likely pathogenic 1

Variant name Variant type Phenotype Germline classification Molecular consequence dbSNP_ID Submitter
NM_016042.4(EXOSC3):c.395A>C (p.Asp132Ala) Single nucleotide variant Hypotonia

 

Congenital pontocerebellar hypoplasia type 1

 

Inborn genetic diseases

 

not provided

 

Pontocerebellar hypoplasia type 1B

 

Abnormality of the nervous system

 

See cases
Pathogenic missense variant rs141138948 .Lifecell International Pvt. Ltd
NM_003384.3(VRK1):c.1159+1G>A Single nucleotide variant Pontocerebellar hypoplasia type 1A

 

Neuronopathy, distal hereditary motor, autosomal recessive 10

 

not provided
Pathogenic/Likely pathogenic splice donor variant rs774877872 .Kasturba Medical College, Manipal, Kasturba Medical College, Manipal, Manipal Academy of Higher Education, Manipal, India
.Neuberg Centre For Genomic Medicine, NCGM

Graph displaying all Indian institutes, the rare genetic disorders they studied, and the variants submitted to ClinVar