GenTIGSA Gene Database on Rare Genetic Disorders

Variants in ClinVar from 539 of 916 Rare Genetic Disorders of GenTIGS

Peroxisome biogenesis disorder

An  Autosomal recessive  mode(s) within the Neurodegenerative disorders  category

Likely pathogenic 3
Uncertain significance 1

Variant name Variant type GRCH38 location Germline classification Molecular consequence dbSNP_ID Submitter
NM_000466.3(PEX1):c.1670+1G>A Single nucleotide variant Chr7:92509328 Likely pathogenic Splice donor variant rs1057517490 .Diagnostics Division, CENTRE FOR DNA FINGERPRINTING AND DIAGNOSTICS
NM_004813.4(PEX16):c.952+3A>G Single nucleotide variant Chr11:45910895 Uncertain significance Intron variant rs2134686616 .Kasturba Medical College, Manipal, Kasturba Medical College, Manipal, Manipal Academy of Higher Education, Manipal, India
NM_001127649.3(PEX26):c.379_380delinsGA (p.Leu127Glu) Indel Chr22:18083444 - 18083445 Likely pathogenic Missense variant rs2517670734 .Lifecell International Pvt. Ltd
NM_003630.3(PEX3):c.844A>C (p.Thr282Pro) Single nucleotide variant Chr6:143479101 Likely pathogenic Missense variant rs1473197986 .Kasturba Medical College, Manipal, Kasturba Medical College, Manipal, Manipal Academy of Higher Education, Manipal, India

Indian Institutes & Variant Submission Overview
Chromosome-wise Variant Distribution