GenTIGSA Gene Database on Rare Genetic Disorders
  Beta Version

Variants from 536 rare genetic disorders, with a total of 897 reported, submitted from India

Niemann-Pick disease, type C1

An  Autosomal recessive  mode(s) within the Metabolic disorders/Lysosomal storage disorders  category

Likely pathogenic 2
Pathogenic 2
Uncertain significance 1

Variant name Variant type GRCH38 location Germline classification Molecular consequence dbSNP_ID Submitter
NM_000271.5(NPC1):c.3246T>A (p.Ser1082Arg) Single nucleotide variant Chr18:23535700 Likely pathogenic Missense variant rs761952957 .Institute of Medical Genetics and Genomics, Sir Ganga Ram Hospital
NM_000271.5(NPC1):c.1522G>A (p.Asp508Asn) Single nucleotide variant Chr18:23554789 Uncertain significance Missense variant rs756587493 .Institute of Medical Genetics and Genomics, Sir Ganga Ram Hospital
NM_000271.5(NPC1):c.1418C>G (p.Ser473Ter) Single nucleotide variant Chr18:23554893 Pathogenic Nonsense rs2511276304 .Department of Medical Genetics, Sanjay Gandhi Post Graduate Institute of Medical Sciences
NM_000271.5(NPC1):c.1454_1459del (p.Leu485_Asn486del) Deletion Chr18:23554852 - 23554857 Likely pathogenic Inframe_deletion rs2511275904 .Department of Medical Genetics, Sanjay Gandhi Post Graduate Institute of Medical Sciences
NM_000543.5(SMPD1):c.1252C>T (p.Arg418Ter) Single nucleotide variant Chr11:6393376 Pathogenic Nonsense|non-coding transcript variant|intron variant rs755160837 .Diagnostics Division, CENTRE FOR DNA FINGERPRINTING AND DIAGNOSTICS
.Kasturba Medical College, Manipal, Kasturba Medical College, Manipal, Manipal Academy of Higher Education, Manipal, India
.Neuberg Centre For Genomic Medicine, NCGM

Graph displaying all Indian institutes, the rare genetic disorders they studied, and the variants submitted to ClinVar