GenTIGSA Gene Database on Rare Genetic Disorders

Variants in ClinVar from 539 of 916 Rare Genetic Disorders of GenTIGS

Neurodegeneration with brain iron accumulation

An  Autosomal dominant, Autosomal recessive  mode(s) within the Neurodegenerative disorders  category

Conflicting classifications of pathogenicity 2
Likely pathogenic 2
Pathogenic 1
Pathogenic/Likely pathogenic 5
Uncertain significance 6

Variant name Variant type GRCH38 location Germline classification Molecular consequence dbSNP_ID Submitter
NM_031448.6(C19orf12):c.163G>T (p.Gly55Trp) Single nucleotide variant Chr19:29702975 Uncertain significance Missense variant|5 prime UTR variant .Pediatrics Genetics, Post Graduate Institute of Medical Education and Research
NM_031448.6(C19orf12):c.-10-1G>A Single nucleotide variant Chr19:29708424 Likely pathogenic Intron variant|splice acceptor variant .Institute of Bioinformatics
NM_031448.6(C19orf12):c.118T>G (p.Phe40Val) Single nucleotide variant Chr19:29708296 Conflicting classifications of pathogenicity Missense variant|5 prime UTR variant|intron variant rs2513299932 .Institute of Bioinformatics
.Neuberg Centre For Genomic Medicine, NCGM
NM_031448.6(C19orf12):c.415T>C (p.Tyr139His) Single nucleotide variant Chr19:29702723 Uncertain significance Missense variant|3 prime UTR variant rs753880224 .Foundation for Research in Genetics and Endocrinology, FRIGE's Institute of Human Genetics
NM_031448.6(C19orf12):c.146C>T (p.Pro49Leu) Single nucleotide variant Chr19:29708268 Uncertain significance Missense variant|5 prime UTR variant|intron variant rs1424999393 .Institute of Bioinformatics
NM_031448.6(C19orf12):c.332T>C (p.Val111Ala) Single nucleotide variant Chr19:29702806 Uncertain significance Missense variant|intron variant rs1972173461 .Foundation for Research in Genetics and Endocrinology, FRIGE's Institute of Human Genetics
NM_031448.6(C19orf12):c.46T>C (p.Ser16Pro) Single nucleotide variant Chr19:29708368 Uncertain significance Missense variant|5 prime UTR variant|intron variant rs1568332606 .Foundation for Research in Genetics and Endocrinology, FRIGE's Institute of Human Genetics
NM_031448.6(C19orf12):c.161-2del Deletion Chr19:29702979 Conflicting classifications of pathogenicity Splice acceptor variant rs1352744778 .Institute of Bioinformatics
NM_031448.6(C19orf12):c.215C>T (p.Pro72Leu) Single nucleotide variant Chr19:29702923 Likely pathogenic Missense variant rs201987973 .Kasturba Medical College, Manipal, Kasturba Medical College, Manipal, Manipal Academy of Higher Education, Manipal, India
NM_031448.6(C19orf12):c.-2C>T Single nucleotide variant Chr19:29708415 Pathogenic/Likely pathogenic 5 prime UTR variant|intron variant rs397514477 .Institute of Bioinformatics
NM_025233.7(COASY):c.1486-3C>G Single nucleotide variant Chr17:42565656 Pathogenic/Likely pathogenic Intron variant rs577714887 .Department of Medical Genetics, Sanjay Gandhi Post Graduate Institute of Medical Sciences
.Institute of Medical Genetics and Genomics, Sir Ganga Ram Hospital
.Kasturba Medical College, Manipal, Kasturba Medical College, Manipal, Manipal Academy of Higher Education, Manipal, India
.Neuberg Centre For Genomic Medicine, NCGM
NM_003560.4(PLA2G6):c.2239C>T (p.Arg747Trp) Single nucleotide variant Chr22:38112541 Pathogenic/Likely pathogenic Missense variant rs121908687 .Lifecell International Pvt. Ltd
NM_003560.4(PLA2G6):c.2222G>A (p.Arg741Gln) Single nucleotide variant Chr22:38112558 Pathogenic/Likely pathogenic Missense variant rs121908686 .Foundation for Research in Genetics and Endocrinology, FRIGE's Institute of Human Genetics
.Neuberg Centre For Genomic Medicine, NCGM
NM_001029896.2(WDR45):c.516+26G>A Single nucleotide variant ChrX:49075840 Uncertain significance Intron variant .Kasturba Medical College, Manipal, Kasturba Medical College, Manipal, Manipal Academy of Higher Education, Manipal, India
NM_001029896.2(WDR45):c.827+1G>C Single nucleotide variant ChrX:49075363 Pathogenic Splice donor variant rs1557083958 .Lifecell International Pvt. Ltd
NM_001029896.2(WDR45):c.516+1_516+3del Microsatellite ChrX:49075863 - 49075865 Pathogenic/Likely pathogenic Splice donor variant rs1557084113 .Kasturba Medical College, Manipal, Kasturba Medical College, Manipal, Manipal Academy of Higher Education, Manipal, India

Indian Institutes & Variant Submission Overview
Chromosome-wise Variant Distribution