GenTIGSA Gene Database on Rare Genetic Disorders

Variants in ClinVar from 539 of 916 Rare Genetic Disorders of GenTIGS

Methylmalonic acidemia

An  Autosomal recessive  mode(s) within the Metabolic disorders  category

Conflicting classifications of pathogenicity 1
Pathogenic 1
Pathogenic/Likely pathogenic 1
Uncertain significance 1

Variant name Variant type GRCH38 location Germline classification Molecular consequence dbSNP_ID Submitter
NM_001243279.3(ACSF3):c.1367-464C>T Single nucleotide variant Chr16:89144803 Uncertain significance Intron variant rs2151560692 .Kasturba Medical College, Manipal, Kasturba Medical College, Manipal, Manipal Academy of Higher Education, Manipal, India
NM_001243279.3(ACSF3):c.1412G>A (p.Arg471Gln) Single nucleotide variant Chr16:89145312 Conflicting classifications of pathogenicity Missense variant|non-coding transcript variant rs387907119 .Kasturba Medical College, Manipal, Kasturba Medical College, Manipal, Manipal Academy of Higher Education, Manipal, India
NM_172250.3(MMAA):c.433C>T (p.Arg145Ter) Single nucleotide variant Chr4:145639572 Pathogenic/Likely pathogenic Nonsense rs104893851 .Foundation for Research in Genetics and Endocrinology, FRIGE's Institute of Human Genetics
NM_052845.4(MMAB):c.197-1G>T Single nucleotide variant Chr12:109568864 Pathogenic Splice acceptor variant rs763935916 .Foundation for Research in Genetics and Endocrinology, FRIGE's Institute of Human Genetics

Indian Institutes & Variant Submission Overview
Chromosome-wise Variant Distribution