GenTIGSA Gene Database on Rare Genetic Disorders
  Beta Version

Variants from 536 rare genetic disorders, with a total of 897 reported, submitted from India

Megalencephalic leukoencephalopathy with subcortical cysts

An  Autosomal dominant, Autosomal recessive  mode(s) within the Neurodegenerative disorders  category

Likely pathogenic 1
Pathogenic 3
Uncertain significance 1

Variant name Variant type GRCH38 location Germline classification Molecular consequence dbSNP_ID Submitter
NM_015166.4(MLC1):c.798C>G (p.Ser266Arg) Single nucleotide variant Chr22:50068529 Likely pathogenic Missense variant|non-coding transcript variant rs777790290 .Lifecell International Pvt. Ltd
NM_015166.4(MLC1):c.368C>T (p.Thr123Ile) Single nucleotide variant Chr22:50079973 Pathogenic Missense variant|non-coding transcript variant|intron variant rs769089143 .Kasturba Medical College, Manipal, Kasturba Medical College, Manipal, Manipal Academy of Higher Education, Manipal, India
NM_015166.4(MLC1):c.177+5G>A Single nucleotide variant Chr22:50084721 Uncertain significance Intron variant rs1555968723 .Foundation for Research in Genetics and Endocrinology, FRIGE's Institute of Human Genetics
NM_015166.4(MLC1):c.714+1G>A Single nucleotide variant Chr22:50074215 Pathogenic Splice donor variant rs761620701 .Kasturba Medical College, Manipal, Kasturba Medical College, Manipal, Manipal Academy of Higher Education, Manipal, India
NM_015166.4(MLC1):c.135dup (p.Cys46fs) Duplication Chr22:50084767 - 50084768 Pathogenic Frameshift variant|non-coding transcript variant|intron variant rs80358241 .Kasturba Medical College, Manipal, Kasturba Medical College, Manipal, Manipal Academy of Higher Education, Manipal, India
.Lifecell International Pvt. Ltd

Graph displaying all Indian institutes, the rare genetic disorders they studied, and the variants submitted to ClinVar