GenTIGSA Gene Database on Rare Genetic Disorders

Variants in ClinVar from 539 of 916 Rare Genetic Disorders of GenTIGS

Limb-girdle muscular dystrophy

An  Autosomal dominant, Autosomal recessive  mode(s) within the Neuromuscular disorders  category

Benign/Likely benign 1
Conflicting classifications of pathogenicity 6
Likely pathogenic 10
Pathogenic 20
Pathogenic/Likely pathogenic 7
Uncertain significance 6

Variant name Variant type GRCH38 location Germline classification Molecular consequence dbSNP_ID Submitter
NM_003494.4(DYSF):c.[1670T>C];[4701C>G] CompoundHeterozygote Chr: Likely pathogenic .Foundation for Research in Genetics and Endocrinology, FRIGE's Institute of Human Genetics
NM_213599.3(ANO5):c.1213C>T (p.Gln405Ter) Single nucleotide variant Chr11:22255403 Pathogenic/Likely pathogenic Nonsense rs368970223 .Lifecell International Pvt. Ltd
NM_000070.3(CAPN3):c.2439+1G>T Single nucleotide variant Chr15:42411346 Likely pathogenic Splice donor variant rs867531606 .Kasturba Medical College, Manipal, Kasturba Medical College, Manipal, Manipal Academy of Higher Education, Manipal, India
NM_000070.3(CAPN3):c.2309A>G (p.Tyr770Cys) Single nucleotide variant Chr15:42410929 Likely pathogenic Missense variant rs2141225644 .Kasturba Medical College, Manipal, Kasturba Medical College, Manipal, Manipal Academy of Higher Education, Manipal, India
NM_000070.3(CAPN3):c.2217C>G (p.Ser739=) Single nucleotide variant Chr15:42410620 Pathogenic Synonymous variant rs148851444 .Kasturba Medical College, Manipal, Kasturba Medical College, Manipal, Manipal Academy of Higher Education, Manipal, India
NM_000070.3(CAPN3):c.397G>A (p.Ala133Thr) Single nucleotide variant Chr15:42386184 Conflicting classifications of pathogenicity Missense variant rs946415346
NM_000070.3(CAPN3):c.2134_*219del (p.Leu712_Ter822del) Deletion Chr15:42410446 - 42411992 Likely pathogenic Stop lost|splice acceptor variant|splice donor variant|inframe_deletion .Foundation for Research in Genetics and Endocrinology, FRIGE's Institute of Human Genetics
NM_000070.3(CAPN3):c.1621C>T (p.Arg541Trp) Single nucleotide variant Chr15:42402878 Pathogenic/Likely pathogenic Missense variant rs142004418 .Lifecell International Pvt. Ltd
NM_000070.3(CAPN3):c.865C>T (p.Arg289Trp) Single nucleotide variant Chr15:42390016 Pathogenic/Likely pathogenic Missense variant|intron variant rs528417986 .Kasturba Medical College, Manipal, Kasturba Medical College, Manipal, Manipal Academy of Higher Education, Manipal, India
NM_000070.3(CAPN3):c.2305C>T (p.Arg769Trp) Single nucleotide variant Chr15:42410925 Pathogenic/Likely pathogenic Missense variant rs868791726 .Kasturba Medical College, Manipal, Kasturba Medical College, Manipal, Manipal Academy of Higher Education, Manipal, India
NM_000070.3(CAPN3):c.2051-1G>T Single nucleotide variant Chr15:42409930 Pathogenic Splice acceptor variant rs886042108 .Foundation for Research in Genetics and Endocrinology, FRIGE's Institute of Human Genetics
.Lifecell International Pvt. Ltd
.Neuberg Centre For Genomic Medicine, NCGM
NM_000070.3(CAPN3):c.1342C>T (p.Arg448Cys) Single nucleotide variant Chr15:42399640 Pathogenic Missense variant rs776043976 .Kasturba Medical College, Manipal, Kasturba Medical College, Manipal, Manipal Academy of Higher Education, Manipal, India
NM_000070.3(CAPN3):c.802-9G>A Single nucleotide variant Chr15:42389944 Pathogenic Intron variant rs761211705 .Lifecell International Pvt. Ltd
NM_000070.3(CAPN3):c.1343G>A (p.Arg448His) Single nucleotide variant Chr15:42399641 Pathogenic Missense variant rs863224956 .Kasturba Medical College, Manipal, Kasturba Medical College, Manipal, Manipal Academy of Higher Education, Manipal, India
.Neuberg Centre For Genomic Medicine, NCGM
NM_000070.3(CAPN3):c.2338G>C (p.Asp780His) Single nucleotide variant Chr15:42410958 Pathogenic Missense variant rs778768583 .Foundation for Research in Genetics and Endocrinology, FRIGE's Institute of Human Genetics
.Neuberg Centre For Genomic Medicine, NCGM
NM_001101426.4(CRPPA):c.634G>A (p.Glu212Lys) Single nucleotide variant Chr7:16376142 Uncertain significance Missense variant|non-coding transcript variant|intron variant rs2128312068 .Kasturba Medical College, Manipal, Kasturba Medical College, Manipal, Manipal Academy of Higher Education, Manipal, India
NM_058246.4(DNAJB6):c.236G>A (p.Gly79Asp) Single nucleotide variant Chr7:157367373 Likely pathogenic Missense variant rs575938861 .Diagnostics Services (NGS), CSIR - Centre For Cellular And Molecular Biology
NM_001130987.2(DYSF):c.5195G>C (p.Arg1732Pro) Single nucleotide variant Chr2:71665182 Likely pathogenic Missense variant rs779987458 .Institute of Medical Genetics and Genomics, Sir Ganga Ram Hospital
NM_001130987.2(DYSF):c.3433_3434dup (p.Met1146fs) Duplication Chr2:71589622 - 71589623 Likely pathogenic Frameshift variant rs2545988788 .Lifecell International Pvt. Ltd
NM_001130987.2(DYSF):c.147+1G>A Single nucleotide variant Chr2:71480939 Pathogenic Splice donor variant rs2082833010 .Diagnostics Services (NGS), CSIR - Centre For Cellular And Molecular Biology
NM_001130987.2(DYSF):c.5405del (p.Glu1802fs) Deletion Chr2:71667463 Pathogenic Frameshift variant rs2095035479 .Diagnostics Services (NGS), CSIR - Centre For Cellular And Molecular Biology
NM_001130987.2(DYSF):c.1721T>C (p.Leu574Pro) Single nucleotide variant Chr2:71551635 Pathogenic Missense variant rs200916654 .Foundation for Research in Genetics and Endocrinology, FRIGE's Institute of Human Genetics
NM_001130987.2(DYSF):c.4701C>G (p.Tyr1567Ter) Single nucleotide variant Chr2:71656236 Likely pathogenic Nonsense rs770905160 .Foundation for Research in Genetics and Endocrinology, FRIGE's Institute of Human Genetics
NM_001130987.2(DYSF):c.730del (p.Leu244fs) Deletion Chr2:71513892 Pathogenic Frameshift variant rs1553521119 .Foundation for Research in Genetics and Endocrinology, FRIGE's Institute of Human Genetics
NM_001130987.2(DYSF):c.5642G>A (p.Gly1881Asp) Single nucleotide variant Chr2:71669207 Pathogenic Missense variant rs1131692158 .Foundation for Research in Genetics and Endocrinology, FRIGE's Institute of Human Genetics
NM_001130987.2(DYSF):c.2217-1G>T Single nucleotide variant Chr2:71561751 Pathogenic Splice acceptor variant rs886044379 .Foundation for Research in Genetics and Endocrinology, FRIGE's Institute of Human Genetics
NM_001130987.2(DYSF):c.888+1G>A Single nucleotide variant Chr2:71515752 Likely pathogenic Splice donor variant rs886044377 .Neuberg Centre For Genomic Medicine, NCGM
NM_001130987.2(DYSF):c.209T>G (p.Val70Gly) Single nucleotide variant Chr2:71481940 Pathogenic Missense variant rs886042878 .Kasturba Medical College, Manipal, Kasturba Medical College, Manipal, Manipal Academy of Higher Education, Manipal, India
NM_001130987.2(DYSF):c.159G>A (p.Trp53Ter) Single nucleotide variant Chr2:71481890 Pathogenic Nonsense rs886042641 .Kasturba Medical College, Manipal, Kasturba Medical College, Manipal, Manipal Academy of Higher Education, Manipal, India
NM_001130987.2(DYSF):c.2943C>T (p.Gly981=) Single nucleotide variant Chr2:71569898 Conflicting classifications of pathogenicity Synonymous variant rs886042637 .Human Genome Lab, NIMHANS, National Institute of Mental Health and Neuro Sciences
NM_001130987.2(DYSF):c.4254dup (p.Ile1419fs) Duplication Chr2:71612666 - 71612667 Pathogenic Frameshift variant rs398123786 .Lifecell International Pvt. Ltd
.Neuberg Centre For Genomic Medicine, NCGM
NM_001130987.2(DYSF):c.3191G>A (p.Arg1064His) Single nucleotide variant Chr2:71570704 Pathogenic Missense variant rs121908958 .Kasturba Medical College, Manipal, Kasturba Medical College, Manipal, Manipal Academy of Higher Education, Manipal, India
.Neuberg Centre For Genomic Medicine, NCGM
NM_001079802.2(FKTN):c.165+5G>A Single nucleotide variant Chr9:105596662 Conflicting classifications of pathogenicity Intron variant rs2132596368 .Kasturba Medical College, Manipal, Kasturba Medical College, Manipal, Manipal Academy of Higher Education, Manipal, India
.Neuberg Centre For Genomic Medicine, NCGM
NM_021971.4(GMPPB):c.358A>G (p.Met120Val) Single nucleotide variant Chr3:49723016 Pathogenic Missense variant rs1559697515 .Human Genome Lab, NIMHANS, National Institute of Mental Health and Neuro Sciences
NM_021971.4(GMPPB):c.1000G>A (p.Asp334Asn) Single nucleotide variant Chr3:49721835 Pathogenic/Likely pathogenic Missense variant rs397509422 .Foundation for Research in Genetics and Endocrinology, FRIGE's Institute of Human Genetics
.Kasturba Medical College, Manipal, Kasturba Medical College, Manipal, Manipal Academy of Higher Education, Manipal, India
.Neuberg Centre For Genomic Medicine, NCGM
NM_001267550.2(TTN):c.48953T>C (p.Ile16318Thr) Single nucleotide variant Chr2:178614561 Conflicting classifications of pathogenicity Missense variant|non-coding transcript variant rs72677243 .Foundation for Research in Genetics and Endocrinology, FRIGE's Institute of Human Genetics
NM_000232.5(SGCB):c.3G>T (p.Met1Ile) Single nucleotide variant Chr4:52038257 Pathogenic Missense variant|initiator_codon_variant rs2109380946 .Kasturba Medical College, Manipal, Kasturba Medical College, Manipal, Manipal Academy of Higher Education, Manipal, India
NM_201384.3(PLEC):c.5933A>C (p.Glu1978Ala) Single nucleotide variant Chr8:143923996 Uncertain significance Missense variant rs782017511 .Foundation for Research in Genetics and Endocrinology, FRIGE's Institute of Human Genetics
NM_201384.3(PLEC):c.2587CAGGAGGCC[1] (p.863QEA[1]) Microsatellite Chr8:143930152 - 143930160 Conflicting classifications of pathogenicity Inframe_deletion rs786205252 .Kasturba Medical College, Manipal, Kasturba Medical College, Manipal, Manipal Academy of Higher Education, Manipal, India
NM_013382.7(POMT2):c.512C>T (p.Ser171Leu) Single nucleotide variant Chr14:77304727 Uncertain significance Missense variant rs750346960 .Kasturba Medical College, Manipal, Kasturba Medical College, Manipal, Manipal Academy of Higher Education, Manipal, India
NM_013382.7(POMT2):c.1364G>A (p.Arg455Gln) Single nucleotide variant Chr14:77285601 Uncertain significance Missense variant rs757110456 .Kasturba Medical College, Manipal, Kasturba Medical College, Manipal, Manipal Academy of Higher Education, Manipal, India
NM_013382.7(POMT2):c.884C>G (p.Thr295Arg) Single nucleotide variant Chr14:77299494 Uncertain significance Missense variant rs794727871 .Pediatrics Genetics, Post Graduate Institute of Medical Education and Research
NM_000232.5(SGCB):c.621+3A>G Single nucleotide variant Chr4:52028727 Uncertain significance Intron variant .Kasturba Medical College, Manipal, Kasturba Medical College, Manipal, Manipal Academy of Higher Education, Manipal, India
NM_000232.5(SGCB):c.271C>T (p.Arg91Cys) Single nucleotide variant Chr4:52029836 Pathogenic Missense variant rs555514820 .Kasturba Medical College, Manipal, Kasturba Medical College, Manipal, Manipal Academy of Higher Education, Manipal, India
NM_000231.3(SGCG):c.195+4_195+7del Microsatellite Chr13:23203889 - 23203892 Pathogenic Splice donor variant rs797045106
NM_017739.4(POMGNT1):c.1100G>A (p.Arg367His) Single nucleotide variant Chr1:46193315 Conflicting classifications of pathogenicity Missense variant rs762972459 .Kasturba Medical College, Manipal, Kasturba Medical College, Manipal, Manipal Academy of Higher Education, Manipal, India
.Neuberg Centre For Genomic Medicine, NCGM
NM_001267550.2(TTN):c.62129dup (p.Ser20712fs) Duplication Chr2:178589595 - 178589596 Likely pathogenic Frameshift variant rs886039913 .Diagnostics Division, CENTRE FOR DNA FINGERPRINTING AND DIAGNOSTICS
NM_001267550.2(TTN):c.61555C>T (p.Arg20519Ter) Single nucleotide variant Chr2:178590170 Pathogenic/Likely pathogenic Nonsense rs794729278 .Lifecell International Pvt. Ltd
NM_001267550.2(TTN):c.104576G>A (p.Arg34859Gln) Single nucleotide variant Chr2:178532039 Benign/Likely benign Missense variant rs68080670 .Foundation for Research in Genetics and Endocrinology, FRIGE's Institute of Human Genetics
NM_006009.4(TUBA1A):c.1204C>T (p.Arg402Cys) Single nucleotide variant Chr12:49185162 Pathogenic/Likely pathogenic Missense variant rs587784483 .Lifecell International Pvt. Ltd
.Suma Genomics

Indian Institutes & Variant Submission Overview
Chromosome-wise Variant Distribution