GenTIGSA Gene Database on Rare Genetic Disorders

Variants in ClinVar from 539 of 916 Rare Genetic Disorders of GenTIGS

Hermansky-Pudlak syndrome 1

An  Autosomal recessive  mode(s) within the Multisystemic disorders  category

Likely pathogenic 1
Pathogenic 1
Pathogenic/Likely pathogenic 1
Uncertain significance 1

Variant name Variant type GRCH38 location Germline classification Molecular consequence dbSNP_ID Submitter
NM_001261826.3(AP3D1):c.3134C>T (p.Ser1045Phe) Single nucleotide variant Chr19:2110748 Uncertain significance Missense variant rs768412125 .Prabudh Goel Research Team, All India Institute Medical Sciences, New Delhi
NM_000195.5(HPS1):c.1657C>T (p.Gln553Ter) Single nucleotide variant Chr10:98422455 Pathogenic/Likely pathogenic Nonsense rs1591031929 .Diagnostics Services (NGS), CSIR - Centre For Cellular And Molecular Biology
NM_000195.5(HPS1):c.507+2T>G Single nucleotide variant Chr10:98433981 Likely pathogenic 5 prime UTR variant|synonymous variant|missense variant|splice donor variant rs1591109881 .Diagnostics Services (NGS), CSIR - Centre For Cellular And Molecular Biology
NM_000195.5(HPS1):c.972del (p.Met325fs) Deletion Chr10:98427230 Pathogenic Frameshift variant|5 prime UTR variant rs281865082 .Kasturba Medical College, Manipal, Kasturba Medical College, Manipal, Manipal Academy of Higher Education, Manipal, India

Indian Institutes & Variant Submission Overview
Chromosome-wise Variant Distribution