GenTIGSA Gene Database on Rare Genetic Disorders

Variants in ClinVar from 539 of 916 Rare Genetic Disorders of GenTIGS

Gaucher disease

An  Autosomal recessive  mode(s) within the Metabolic disorders/Lysosomal storage disorders  category

Conflicting classifications of pathogenicity 2
Likely pathogenic 9
Pathogenic 3
Pathogenic; risk factor 1
Pathogenic/Likely pathogenic 3
Uncertain significance 2

Variant name Variant type GRCH38 location Germline classification Molecular consequence dbSNP_ID Submitter
NM_000157.3(GBA1):c.[1197G>T];[1603C>T] CompoundHeterozygote Chr: Likely pathogenic .Foundation for Research in Genetics and Endocrinology, FRIGE's Institute of Human Genetics
NM_000157.3(GBA1):c.[1448T>C];[167T>G] CompoundHeterozygote Chr: Likely pathogenic .Foundation for Research in Genetics and Endocrinology, FRIGE's Institute of Human Genetics
NM_000157.3(GBA1):c.[1448T>C];[407C>T] CompoundHeterozygote Chr: Likely pathogenic .Foundation for Research in Genetics and Endocrinology, FRIGE's Institute of Human Genetics
NM_000157.4(GBA1):c.538G>A (p.Asp180Asn) Single nucleotide variant Chr1:155238567 Likely pathogenic Missense variant rs1285705042 .Kasturba Medical College, Manipal, Kasturba Medical College, Manipal, Manipal Academy of Higher Education, Manipal, India
NM_000157.4(GBA1):c.827C>T (p.Ser276Phe) Single nucleotide variant Chr1:155237513 Conflicting classifications of pathogenicity Missense variant rs755512507
NM_000157.4(GBA1):c.970C>T (p.Arg324Cys) Single nucleotide variant Chr1:155237370 Conflicting classifications of pathogenicity Missense variant rs765633380
NM_000157.4(GBA1):c.1316G>A (p.Ser439Asn) Single nucleotide variant Chr1:155235753 Uncertain significance Missense variant rs1571966221 .Diagnostics Services (NGS), CSIR - Centre For Cellular And Molecular Biology
NM_000157.4(GBA1):c.1603C>T (p.Arg535Cys) Single nucleotide variant Chr1:155235003 Pathogenic Missense variant rs747506979 .Foundation for Research in Genetics and Endocrinology, FRIGE's Institute of Human Genetics
.Neuberg Centre For Genomic Medicine, NCGM
NM_000157.4(GBA1):c.866G>C (p.Gly289Ala) Single nucleotide variant Chr1:155237474 Likely pathogenic Missense variant rs878853321 .Foundation for Research in Genetics and Endocrinology, FRIGE's Institute of Human Genetics
NM_000157.4(GBA1):c.1397T>G (p.Ile466Ser) Single nucleotide variant Chr1:155235303 Likely pathogenic Missense variant rs878853320 .Foundation for Research in Genetics and Endocrinology, FRIGE's Institute of Human Genetics
NM_000157.4(GBA1):c.1459G>A (p.Ala487Thr) Single nucleotide variant Chr1:155235241 Likely pathogenic Missense variant rs878853317 .Foundation for Research in Genetics and Endocrinology, FRIGE's Institute of Human Genetics
NM_000157.4(GBA1):c.1177C>G (p.Leu393Val) Single nucleotide variant Chr1:155236292 Likely pathogenic Missense variant rs878853315 .Foundation for Research in Genetics and Endocrinology, FRIGE's Institute of Human Genetics
NM_000157.4(GBA1):c.415G>C (p.Ala139Pro) Single nucleotide variant Chr1:155239655 Likely pathogenic Missense variant|intron variant rs878853314 .Foundation for Research in Genetics and Endocrinology, FRIGE's Institute of Human Genetics
NM_000157.4(GBA1):c.1448T>G (p.Leu483Arg) Single nucleotide variant Chr1:155235252 Pathogenic/Likely pathogenic Missense variant rs421016 .Foundation for Research in Genetics and Endocrinology, FRIGE's Institute of Human Genetics
NM_000157.4(GBA1):c.160G>T (p.Val54Leu) Single nucleotide variant Chr1:155240033 Pathogenic Missense variant|5 prime UTR variant rs121908302 .Foundation for Research in Genetics and Endocrinology, FRIGE's Institute of Human Genetics
NM_000157.4(GBA1):c.1504C>T (p.Arg502Cys) Single nucleotide variant Chr1:155235196 Pathogenic Missense variant rs80356771 .Foundation for Research in Genetics and Endocrinology, FRIGE's Institute of Human Genetics
NM_000157.4(GBA1):c.1342G>C (p.Asp448His) Single nucleotide variant Chr1:155235727 Pathogenic/Likely pathogenic Missense variant rs1064651 .Foundation for Research in Genetics and Endocrinology, FRIGE's Institute of Human Genetics
.Lifecell International Pvt. Ltd
NM_000157.4(GBA1):c.1448T>C (p.Leu483Pro) Single nucleotide variant Chr1:155235252 Pathogenic; risk factor Missense variant rs421016 .Foundation for Research in Genetics and Endocrinology, FRIGE's Institute of Human Genetics
.Kasturba Medical College, Manipal, Kasturba Medical College, Manipal, Manipal Academy of Higher Education, Manipal, India
.Neuberg Centre For Genomic Medicine, NCGM
NM_000157.4(GBA1):c.835C>G (p.Leu279Val) Single nucleotide variant Chr1:155237505 Uncertain significance Missense variant rs1057519020 .Foundation for Research in Genetics and Endocrinology, FRIGE's Institute of Human Genetics
NM_002778.4(PSAP):c.679_681del (p.Lys227del) Deletion Chr10:71828053 - 71828055 Pathogenic/Likely pathogenic Inframe_deletion rs1431844269 .Foundation for Research in Genetics and Endocrinology, FRIGE's Institute of Human Genetics
.Kasturba Medical College, Manipal, Kasturba Medical College, Manipal, Manipal Academy of Higher Education, Manipal, India
.Neuberg Centre For Genomic Medicine, NCGM

Indian Institutes & Variant Submission Overview
Chromosome-wise Variant Distribution