GenTIGSA Gene Database on Rare Genetic Disorders
  Beta Version

Variants from 536 rare genetic disorders, with a total of 897 reported, submitted from India

Congenital myasthenic syndrome 10

An  Autosomal recessive  mode(s) within the Neuromuscular disorders  category

Conflicting classifications of pathogenicity 1
Likely pathogenic 1
Pathogenic 3
Pathogenic/Likely pathogenic 2

Variant name Variant type GRCH38 location Germline classification Molecular consequence dbSNP_ID Submitter
NM_173660.5(DOK7):c.533-2A>G Single nucleotide variant Chr4:3485537 Conflicting classifications of pathogenicity Splice acceptor variant rs2475052844
NM_173660.5(DOK7):c.1511_1513del (p.Pro504_Ter505delinsArg) Deletion Chr4:3493497 - 3493499 Likely pathogenic 3 prime UTR variant|stop lost|intron variant rs762345055
NM_173660.5(DOK7):c.483_484dup (p.Ala162fs) Duplication Chr4:3476490 - 3476491 Pathogenic Frameshift variant|intron variant rs1577153124 .Diagnostics Services (NGS), CSIR - Centre For Cellular And Molecular Biology
NM_173660.5(DOK7):c.1061C>T (p.Ser354Phe) Single nucleotide variant Chr4:3493047 Pathogenic 3 prime UTR variant|missense variant rs756015202 .Foundation for Research in Genetics and Endocrinology, FRIGE's Institute of Human Genetics
NM_173660.5(DOK7):c.199C>T (p.Pro67Ser) Single nucleotide variant Chr4:3473504 Pathogenic Missense variant|intron variant rs1553846331 .Foundation for Research in Genetics and Endocrinology, FRIGE's Institute of Human Genetics
NM_173660.5(DOK7):c.1378dup (p.Gln460fs) Duplication Chr4:3493358 - 3493359 Pathogenic/Likely pathogenic 3 prime UTR variant|frameshift variant rs606231133 .Department of Medical Genetics, Sanjay Gandhi Post Graduate Institute of Medical Sciences
NM_173660.5(DOK7):c.1263dup (p.Ser422fs) Duplication Chr4:3493242 - 3493243 Pathogenic/Likely pathogenic Frameshift variant|3 prime UTR variant rs606231129 .Kasturba Medical College, Manipal, Kasturba Medical College, Manipal, Manipal Academy of Higher Education, Manipal, India

Graph displaying all Indian institutes, the rare genetic disorders they studied, and the variants submitted to ClinVar