GenTIGSA Gene Database on Rare Genetic Disorders

Variants in ClinVar from 582 of 1004 Rare Genetic Disorders of GenTIGS

Canavan disease

An  Autosomal recessive  mode(s) within the Neurodegenerative disorders  category

Pathogenic/Likely pathogenic 3

Variant name Variant type GRCH38 location Germline classification Molecular consequence dbSNP_ID Submitter
NM_000049.4(ASPA):c.526G>A (p.Gly176Ser) Single nucleotide variant Chr17:3483592 Pathogenic/Likely pathogenic Missense variant|intron variant rs2150748728 .Clinical Genetics Laboratory, Christian Medical College, Vellore
NM_000049.4(ASPA):c.503G>A (p.Arg168His) Single nucleotide variant Chr17:3483569 Pathogenic/Likely pathogenic Missense variant|intron variant rs770706390 .Lifecell International Pvt. Ltd
.Neuberg Centre For Genomic Medicine, NCGM
NM_000049.4(ASPA):c.454T>C (p.Cys152Arg) Single nucleotide variant Chr17:3483520 Pathogenic/Likely pathogenic Missense variant|intron variant rs104894548 .Foundation for Research in Genetics and Endocrinology, FRIGE's Institute of Human Genetics

Indian Institutes & Variant Submission Overview
Chromosome-wise Variant Distribution