GenTIGSA Gene Database on Rare Genetic Disorders

Variants in ClinVar from 539 of 916 Rare Genetic Disorders of GenTIGS

Amyotrophic lateral sclerosis

An  Autosomal dominant, Autosomal recessive  mode(s) within the Neuromuscular disorders  category

Conflicting classifications of pathogenicity 2
Likely pathogenic 9
Pathogenic 8
Pathogenic/Likely pathogenic 6

Variant name Variant type GRCH38 location Germline classification Molecular consequence dbSNP_ID Submitter
NM_020919.4(ALS2):c.2707dup (p.Met903fs) Duplication Chr2:201729056 - 201729057 Pathogenic Frameshift variant rs2106012637 .Medical Genetics, Christian Medical College
NM_020919.4(ALS2):c.4223T>A (p.Leu1408Ter) Single nucleotide variant Chr2:201709938 Pathogenic Nonsense rs2105972075 .Medical Genetics, Christian Medical College
NM_020919.4(ALS2):c.3415C>T (p.Arg1139Ter) Single nucleotide variant Chr2:201724392 Pathogenic/Likely pathogenic Nonsense rs767350733 .Foundation for Research in Genetics and Endocrinology, FRIGE's Institute of Human Genetics
NM_004960.4(FUS):c.1468dup (p.Asp490fs) Duplication Chr16:31191033 - 31191034 Likely pathogenic Frameshift variant|non-coding transcript variant rs2544279181 .Department of Research, Sir Ganga Ram Hospital
NM_001199397.3(NEK1):c.1957C>T (p.Arg653Ter) Single nucleotide variant Chr4:169507087 Pathogenic Nonsense|non-coding transcript variant|intron variant rs773156346 .Kasturba Medical College, Manipal, Kasturba Medical College, Manipal, Manipal Academy of Higher Education, Manipal, India
NM_015046.7(SETX):c.6292C>T (p.Arg2098Ter) Single nucleotide variant Chr9:132288268 Pathogenic Nonsense rs770684782 .Lifecell International Pvt. Ltd
NM_000454.5(SOD1):c.358G>T (p.Val120Phe) Single nucleotide variant Chr21:31668471 Likely pathogenic Missense variant .Human Genome Lab, NIMHANS, National Institute of Mental Health and Neuro Sciences
NM_000454.5(SOD1):c.203T>C (p.Leu68Pro) Single nucleotide variant Chr21:31666482 Likely pathogenic Missense variant .Human Genome Lab, NIMHANS, National Institute of Mental Health and Neuro Sciences
NM_000454.5(SOD1):c.68A>G (p.Gln23Arg) Single nucleotide variant Chr21:31659837 Likely pathogenic Non-coding transcript variant|missense variant .Human Genome Lab, NIMHANS, National Institute of Mental Health and Neuro Sciences
NM_000454.5(SOD1):c.194T>G (p.Phe65Cys) Single nucleotide variant Chr21:31666473 Likely pathogenic Missense variant .Human Genome Lab, NIMHANS, National Institute of Mental Health and Neuro Sciences
NM_000454.5(SOD1):c.281_283dup (p.Gly94_Val95insGly) Duplication Chr21:31667296 - 31667297 Likely pathogenic .Human Genome Lab, NIMHANS, National Institute of Mental Health and Neuro Sciences
NM_000454.5(SOD1):c.455T>A (p.Ile152Asn) Single nucleotide variant Chr21:31668568 Likely pathogenic Missense variant .Human Genome Lab, NIMHANS, National Institute of Mental Health and Neuro Sciences
NM_000454.5(SOD1):c.43G>C (p.Val15Leu) Single nucleotide variant Chr21:31659812 Pathogenic/Likely pathogenic Missense variant rs1568807400 .Human Genome Lab, NIMHANS, National Institute of Mental Health and Neuro Sciences
.Neuberg Centre For Genomic Medicine, NCGM
NM_000454.5(SOD1):c.43G>A (p.Val15Met) Single nucleotide variant Chr21:31659812 Pathogenic/Likely pathogenic Missense variant rs1568807400 .Human Genome Lab, NIMHANS, National Institute of Mental Health and Neuro Sciences
NM_000454.5(SOD1):c.262G>A (p.Val88Met) Single nucleotide variant Chr21:31667280 Pathogenic/Likely pathogenic Missense variant rs1568810641 .Human Genome Lab, NIMHANS, National Institute of Mental Health and Neuro Sciences
NM_000454.5(SOD1):c.255G>C (p.Leu85Phe) Single nucleotide variant Chr21:31667273 Pathogenic/Likely pathogenic Missense variant rs1315541036 .Human Genome Lab, NIMHANS, National Institute of Mental Health and Neuro Sciences
NM_000454.5(SOD1):c.317C>T (p.Ser106Leu) Single nucleotide variant Chr21:31667335 Pathogenic/Likely pathogenic Missense variant rs1378590183 .Human Genome Lab, NIMHANS, National Institute of Mental Health and Neuro Sciences
NM_000454.5(SOD1):c.397GAA[1] (p.Glu134del) Microsatellite Chr21:31668510 - 31668512 Conflicting classifications of pathogenicity Inframe_deletion rs1568811423 .Human Genome Lab, NIMHANS, National Institute of Mental Health and Neuro Sciences
NM_000454.5(SOD1):c.268G>A (p.Ala90Thr) Single nucleotide variant Chr21:31667286 Conflicting classifications of pathogenicity Missense variant rs1568810660
NM_000454.5(SOD1):c.37G>C (p.Gly13Arg) Single nucleotide variant Chr21:31659806 Likely pathogenic Missense variant rs121912456 .Human Genome Lab, NIMHANS, National Institute of Mental Health and Neuro Sciences
NM_000454.5(SOD1):c.256G>C (p.Gly86Arg) Single nucleotide variant Chr21:31667274 Pathogenic Missense variant rs121912436 .Human Genome Lab, NIMHANS, National Institute of Mental Health and Neuro Sciences
NM_000454.5(SOD1):c.131A>G (p.His44Arg) Single nucleotide variant Chr21:31663848 Pathogenic Missense variant rs121912435 .Human Genome Lab, NIMHANS, National Institute of Mental Health and Neuro Sciences
NM_025137.4(SPG11):c.2716del (p.Gln906fs) Deletion Chr15:44620308 Pathogenic Frameshift variant rs312262747 .Lifecell International Pvt. Ltd
.Neuberg Centre For Genomic Medicine, NCGM
NM_025137.4(SPG11):c.733_734del (p.Met245fs) Deletion Chr15:44657230 - 44657231 Pathogenic Frameshift variant rs312262720 .Foundation for Research in Genetics and Endocrinology, FRIGE's Institute of Human Genetics
.Neuberg Centre For Genomic Medicine, NCGM
NM_007126.5(VCP):c.553G>A (p.Glu185Lys) Single nucleotide variant Chr9:35065274 Likely pathogenic Missense variant rs864309501 .Kasturba Medical College, Manipal, Kasturba Medical College, Manipal, Manipal Academy of Higher Education, Manipal, India

Indian Institutes & Variant Submission Overview
Chromosome-wise Variant Distribution