GenTIGSA Gene Database on Rare Genetic Disorders

Monogenic disorders list  

List of monogenic disorders and their associated genes
Monogenic disorders arise from mutations in a single gene, but variations within that gene or in multiple genes can also lead to similar phenotypes, typically following Mendelian inheritance patterns associated with specific genetic changes.

View information by inheritance mode


S.No.  Genetic Disorders
Modes of inheritance
Category Gene symbol Indian
context
 Links
311 Myopathy, lactic acidosis, and sideroblastic anemia 1 
Autosomal recessive
Metabolic disorders PUS1 pseudouridine synthase 1
Reports
Updated as of Feb 01, 2025
PubMed
312 Myopathy, tubular aggregate, 1 
Autosomal dominant
Neuromuscular disorders STIM1 stromal interaction molecule 1
Reports
Updated as of Feb 01, 2025
PubMed
313 Myotonic dystrophy type 2 
Autosomal dominant
Neuromuscular disorders CNBP CCHC-type zinc finger nucleic acid binding protein
Reports
Updated as of Nov 30, 2023
PubMed
314 Naegeli-Franceschetti-Jadassohn syndrome 
Autosomal dominant
Skin disorders KRT14 keratin 14
Reports
Updated as of Feb 01, 2024
PubMed
315 Nager syndrome 
Autosomal dominant
Bone disorders SF3B4 splicing factor 3b subunit 4
Reports
Updated as of Feb 01, 2024
PubMed
316 Nail-patella syndrome 
Autosomal dominant
Bone disorders LMX1B LIM homeobox transcription factor 1 beta
Reports
Updated as of Feb 01, 2024
PubMed
317 Nance-Horan syndrome 
X-linked recessive
Eye disorders NHS NHS actin remodeling regulator
Reports
Updated as of Feb 01, 2024
PubMed
318 Naxos disease 
Autosomal recessive
Cardiovascular disorders JUP junction plakoglobin
Reports
Updated as of Feb 01, 2024
PubMed
319 Netherton syndrome 
Autosomal recessive
Skin disorders SPINK5 serine peptidase inhibitor Kazal type 5
Reports
Updated as of Mar 09, 2023
PubMed
320 Neurofibromatosis type 1 
Autosomal dominant
Bone disorders NF1 neurofibromin 1
Reports
Updated as of Sep 05, 2023
PubMed