GenTIGSA Gene Database on Rare Genetic Disorders
  Beta Version

Monogenic disorders list  

List of monogenic disorders and their associated genes
Monogenic disorders arise from mutations in a single gene, but variations within that gene or in multiple genes can also lead to similar phenotypes, typically following Mendelian inheritance patterns associated with specific genetic changes.

View information by inheritance mode


S.No.  Genetic Disorders
Modes of inheritance
Category Gene symbol Indian
context
 Links
121 Chorea-acanthocytosis 
Autosomal recessive
Neurodegenerative disorders VPS13A vacuolar protein sorting 13 homolog A
Reports
Updated as of Sep 15, 2022
PubMed
122 Choroid plexus papilloma 
Autosomal dominant
Cancer disorders TP53 tumor protein p53
Reports
Updated as of Jan 04, 2024
PubMed
123 Choroideremia 
X-linked recessive
Eye disorders CHM CHM Rab escort protein
Reports
Updated as of Jun 12, 2025
PubMed
124 Chronic inflammatory demyelinating polyneuropathy 
Neuromuscular disorders PMP22 peripheral myelin protein 22
Reports
Updated as of Nov 30, 2023
PubMed
125 CK syndrome 
X-linked recessive
Neurodevelopmental disorders NSDHL NAD(P) dependent steroid dehydrogenase-like
Reports
Updated as of Nov 12, 2025
PubMed
126 Classic congenital adrenal hyperplasia due to 21-hydroxylase deficiency 
Autosomal recessive
Endocrine disorders CYP21A2 cytochrome P450 family 21 subfamily A member 2
Reports
Updated as of Sep 08, 2025
PubMed
127 Coffin-Lowry syndrome 
X-linked dominant
Multisystemic disorders RPS6KA3 ribosomal protein S6 kinase A3
Reports
Updated as of Jan 05, 2026
PubMed
128 Cold-induced sweating syndrome 1 
Autosomal recessive
Neuromuscular disorders CRLF1 cytokine receptor like factor 1
Reports
Updated as of Jun 12, 2025
PubMed
129 Combined immunodeficiency due to DOCK8 deficiency 
Autosomal recessive
Immune disorders DOCK8 dedicator of cytokinesis 8
Reports
Updated as of Feb 01, 2025
PubMed
130 Combined oxidative phosphorylation defect type 27 
Autosomal recessive
Metabolic disorders CARS2 cysteinyl-tRNA synthetase 2, mitochondrial
Reports
Updated as of Jul 20, 2024
PubMed