GenTIGSA Gene Database on Rare Genetic Disorders

Monogenic disorders list  

List of monogenic disorders and their associated genes
Monogenic disorders arise from mutations in a single gene, but variations within that gene or in multiple genes can also lead to similar phenotypes, typically following Mendelian inheritance patterns associated with specific genetic changes.

View information by inheritance mode


S.No.  Genetic Disorders
Modes of inheritance
Category Gene symbol Indian
context
 Links
271 Warburg micro syndrome 
Autosomal recessive
Neurodevelopmental disorders RAB3GAP1 RAB3 GTPase activating protein catalytic subunit 1
RAB18 RAB18, member RAS oncogene family
RAB3GAP2 RAB3 GTPase activating non-catalytic protein subunit 2
TBC1D20 TBC1 domain family member 20
Reports
Updated as of Sep 05, 2023
PubMed
272 Wiskott-Aldrich syndrome 
X-linked dominant
Immune disorders WAS WASP actin nucleation promoting factor
WIPF1 WAS/WASL interacting protein family member 1
Reports
Updated as of Sep 05, 2023
PubMed
273 Wolfram syndrome 
Autosomal recessive
Neurodegenerative disorders CISD2 CDGSH iron sulfur domain 2
WFS1 wolframin ER transmembrane glycoprotein
Reports
Updated as of Sep 05, 2023
PubMed
274 X-linked sideroblastic anemia 1 
X-linked recessive
Metabolic disorders ALAS2 5'-aminolevulinate synthase 2
SLC25A38 solute carrier family 25 member 38
Reports
Updated as of Feb 04, 2025
PubMed
275 Xanthinuria type II 
Autosomal recessive
Metabolic disorders MOCOS molybdenum cofactor sulfurase
XDH xanthine dehydrogenase
Reports
Updated as of Jul 20, 2024
PubMed
276 xeroderma pigmentosum 
Autosomal recessive
Skin disorders XPC XPC complex subunit, DNA damage recognition and repair factor
XPA XPA, DNA damage recognition and repair factor
POLH DNA polymerase eta
DDB2 damage specific DNA binding protein 2
ERCC5 ERCC excision repair 5, endonuclease
ERCC4 ERCC excision repair 4, endonuclease catalytic subunit
ERCC3 ERCC excision repair 3, TFIIH core complex helicase subunit
ERCC2 ERCC excision repair 2, TFIIH core complex helicase subunit
Reports
Updated as of Nov 02, 2023
PubMed
277 Yunis-Varon syndrome 
Autosomal recessive
Bone disorders FIG4 FIG4 phosphoinositide 5-phosphatase
VAC14 VAC14 component of PIKFYVE complex
Reports
Updated as of Feb 04, 2025
PubMed
278 Zellweger spectrum disorders 
Multisystemic disorders PEX1 peroxisomal biogenesis factor 1
PEX6 peroxisomal biogenesis factor 6
PEX19 peroxisomal biogenesis factor 19
Reports
Updated as of Feb 01, 2025
PubMed
279 Zimmermann-Laband syndrome 
Autosomal dominant
Multisystemic disorders KCNH1 potassium voltage-gated channel subfamily H member 1
ATP6V1B2 ATPase H+ transporting V1 subunit B2
KCNN3 potassium calcium-activated channel subfamily N member 3
Reports
Updated as of Nov 12, 2025
PubMed